Small Molecule Therapy for Genetic Disease

This book PDF is perfect for those who love Medical genre, written by Jess G. Thoene and published by Cambridge University Press which was released on 23 August 2010 with total hardcover pages null. You could read this book directly on your devices with pdf, epub and kindle format, check detail and related Small Molecule Therapy for Genetic Disease books below.

Small Molecule Therapy for Genetic Disease
Author : Jess G. Thoene
File Size : 51,9 Mb
Publisher : Cambridge University Press
Language : English
Release Date : 23 August 2010
ISBN : 9781139490764
Pages : null pages
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Small Molecule Therapy for Genetic Disease by Jess G. Thoene Book PDF Summary

Thoene summarises the substantial work that has been accomplished in the treatment of inborn errors of metabolism with simple molecules. This handbook will enable interested clinician scientists to rapidly survey the field, thus ascertaining what has been done as well as future directions for therapeutic research. Its important introductory chapters discuss the infrastructure of the field. The book closely analyses the cofactors used to augment the function of defective enzymes and the compounds that are able to utilise an alternative pathway in order to avoid the consequences of the metabolic block present in the patient. Among other therapies, the authors discuss the use of zinc and tetrathiomolybdate to treat Wilson's disease and the use of cysteamine to treat nephropathic cystinosis.

Small Molecule Therapy for Genetic Disease

Thoene summarises the substantial work that has been accomplished in the treatment of inborn errors of metabolism with simple molecules. This handbook will enable interested clinician scientists to rapidly survey the field, thus ascertaining what has been done as well as future directions for therapeutic research. Its important introductory chapters

Get Book
Outlines and Highlights for Small Molecule Therapy for Genetic Disease by Jess Thoene  Isbn

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Those involved in the drug development process face challenges of efficiency and overall sustainability due in part to high research costs, lengthy development timelines, and late-stage drug failures. Novel clinical trial designs that enroll participants based on their genetics represent a potentially disruptive change that could improve patient outcomes, reduce

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Small Molecule Therapy for Genetic Disease

Thoene summarises the substantial work that has been accomplished in the treatment of inborn errors of metabolism with simple molecules. This handbook will enable interested clinician scientists to rapidly survey the field, thus ascertaining what has been done as well as future directions for therapeutic research. Its important introductory chapters

Get Book
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